Craig Mayer, Nick WIlliams, Vojtech Huser
Lister Hill National Center for Biomedical Communications, National Library of Medicine, NIH, Bethesda, MD

See the full regCTG repository at https://github.com/lhncbc/CRI/tree/master/regCTG

To return to the list of conditions and view other reports go to https://lhncbc.github.io/CRI/regCTG/regCTG-condition_report_links.html


Study Counts

Type Study_count
Total_Studies 195
interventional 148
Observational 42
Registry 5

Studies over Time by Start Date

```

Interventional Trials

Intervention Type

intervention_type Study_Count
Drug 75
Drug|placebo 31
Biological 9
Device 9
Other 8
Biological|placebo 2
Drug|Other 2
Genetic 2
Procedure 2
Behavioral 1
Biological|Procedure 1
Device|Other 1
Dietary Supplement 1
Dietary Supplement|placebo 1
Dietary Supplement|placebo|Procedure 1
Genetic|placebo 1
Other|Procedure 1

Count of Studies by Intervention (normalized and mapped)

Interventions over Time

Yearly studies for each intervention by start date

Studies by Country

Country Study_Count
United States 63
United States|Canada 6
Japan 5
NA 5
Canada 4
France 4
Italy 4
United Kingdom 4
Germany 3
Turkey 3
United States|Australia|Canada|Israel|Sweden|United Kingdom 3
Belgium 2
Belgium|France|Italy|United Kingdom 2
Brazil 2
China 2
Korea, Republic of 2
Switzerland 2
Argentina|Belgium|Brazil|Canada|Chile|Czechia|Denmark|France|Germany|Hungary|Italy|Japan|Korea, Republic of|Netherlands|Norway|Poland|Russian Federation|Spain|Taiwan|Turkey 1
Australia|Belgium|France|Germany|Israel|Netherlands|Spain|Turkey|United Kingdom 1
Belgium|Italy|Netherlands|Sweden 1
Canada|Australia|Belgium|France|Germany|Israel|Italy|Spain|Sweden|United Kingdom 1
Denmark 1
France|Italy|Spain|United Kingdom 1
Germany|Netherlands|Spain|Switzerland|United Kingdom 1
Italy|Netherlands 1
Japan|United States|Australia|Brazil|Bulgaria|Canada|China|Hong Kong|India|Jordan|Korea, Republic of|Malaysia|Mexico|Poland|Puerto Rico|Russian Federation|Sri Lanka|Taiwan|Thailand|Turkey 1
Jordan 1
Mexico 1
Spain 1
Sweden 1
United States|Argentina|Australia|Canada|Israel|Italy 1
United States|Australia|Belgium|Brazil|Bulgaria|Canada|Chile|Czechia|France|Germany|Israel|Italy|Korea, Republic of|Poland|Spain|Sweden|Switzerland|Turkey|United Kingdom 1
United States|Australia|Belgium|Brazil|Canada|Chile|Czechia|France|Germany|Israel|Italy|Korea, Republic of|Poland|Spain|Sweden|Switzerland|Turkey|United Kingdom 1
United States|Australia|Belgium|Bulgaria|Canada|Czechia|France|Germany|Greece|Hungary|Israel|Italy|Poland|Spain|Sweden|United Kingdom 1
United States|Australia|Belgium|Canada|Czechia|Greece|Israel|Netherlands|Spain|Sweden|United Kingdom 1
United States|Australia|Belgium|Canada|France|Germany|Israel|Italy|Spain|Sweden|United Kingdom 1
United States|Australia|Canada|Germany|Ireland|Israel|Sweden|United Kingdom 1
United States|Australia|Canada|Germany|Sweden|United Kingdom 1
United States|Austria|Belgium|Bulgaria|France|Germany|Hungary|Ireland|Israel|Italy|Netherlands|Spain|Sweden|Switzerland|United Kingdom 1
United States|Austria|Belgium|France|Germany|Italy|Netherlands|Spain|Sweden|Switzerland 1
United States|Austria|Belgium|France|Germany|Italy|Spain|Switzerland|United Kingdom 1
United States|Belgium|Canada|France|Germany|Israel|Italy|Netherlands|Serbia|Spain|United Kingdom 1
United States|Belgium|Canada|France|Germany|Italy|Netherlands|Spain 1
United States|Belgium|Canada|France|Italy|Netherlands|United Kingdom 1
United States|Belgium|Italy|Spain|United Kingdom 1
United States|Canada|Germany|Italy|United Kingdom 1
United States|Canada|Italy|Japan|Korea, Republic of|Netherlands|New Zealand|Russian Federation|Spain|Sweden|Taiwan 1
United States|Canada|Japan 1
United States|France|Italy|United Kingdom 1

Sites per Study

Site_count Study_Count
1 65
2 12
3 6
4 11
5 4
6 6
7 7
8 1
9 4
10 1
11 3
12 3
13 3
14 1
20 2
21 1
23 2
25 2
27 1
32 1
33 1
37 2
39 1
40 1
44 1
47 1
55 1
58 1
63 1
66 1
86 1

Phase

Phase Study_Count
Phase 2 38
Phase 1 28
Phase 3 26
N/A 25
Phase 1/Phase 2 22
Phase 2/Phase 3 6
Phase 4 2
Early Phase 1 1

Number of Arms

Number_of_Arms Count_of_Studies
1 47
2 58
3 13
4 12
5 3
6 3
9 1
NA 11

Enrollment Metrics by Phase

Measure Early.Phase.1 N.A Phase.1 Phase.1.Phase.2 Phase.2 Phase.2.Phase.3 Phase.3 Phase.4
Min. 30 4.00 1.00000 3.00 6.00000 19.00000 20.00 48.0
1st Qu. 30 23.00 9.25000 6.25 15.00000 35.25000 74.00 53.5
Median 30 42.00 12.00000 16.00 21.00000 45.00000 140.00 59.0
Mean 30 62.12 14.60714 22.50 32.86486 50.83333 145.28 59.0
3rd Qu. 30 64.00 20.00000 23.75 45.00000 59.25000 219.00 64.5
Max. 30 330.00 37.00000 108.00 174.00000 100.00000 266.00 70.0

Trial Group Type

group_type Group_Count
Experimental 197
Active Comparator 36
Placebo Comparator 34
Other 13
No Intervention 11
NA 11
Sham Comparator 1

Intervention Model

intervention_model Study_Count
Parallel Assignment 62
Single Group Assignment 62
Crossover Assignment 10
Sequential Assignment 8
NA 5
Factorial Assignment 1

Primary Purpose

primary_purpose Study_Count
Treatment 120
Diagnostic 5
Other 5
Basic Science 4
Prevention 4
Supportive Care 4
NA 4
Health Services Research 1
Screening 1

Observational Studies

Studies by Country

Country Study_Count
United States 22
Turkey 5
France 3
Denmark 2
Austria 1
China 1
Egypt 1
Egypt|India|Lebanon|Lithuania|Romania|Sri Lanka|United Arab Emirates 1
France|United Kingdom 1
NA 1
Norway 1
Switzerland 1
United Kingdom 1
United States|Australia|Italy 1

Sites per Study

Site_count Study_Count
1 34
2 2
3 3
5 2
11 1

Enrollment Metrics

Measure Observational
Min 9.0000
1st Qu 30.0000
Median 49.0000
Mean 636.4762
3rd Qu 120.0000
Max 20000.0000

Observation Model

observational_model Study_Count
Cohort 20
Other 7
Case-Only 5
Case-Control 3
Case Control 3
NA 2
Case-Crossover 1
Family-Based 1

Time Perspective

time_perspective Study_Count
Prospective 27
Cross-Sectional 9
Other 3
Retrospective 2
NA 1

Registries

Studies by Country

Country Study_Count
United States 2
France|Austria|Czechia|Germany|Greece|Hungary|Israel|Italy|Latvia|Norway|Portugal|Romania|Slovenia|Sweden|United Kingdom 1
Norway 1
Turkey 1

Sites per Study

Site_count Study_Count
1 2
5 1
51 1
70 1

Enrollment Metrics

Measure Registries
Min 73
1st Qu 270
Median 327
Mean 2434
3rd Qu 1500
Max 10000

Registry Model

observational_model Study_Count
Cohort 4
Other 1

Time Perspective

time_perspective Study_Count
Prospective 4
Cross-Sectional 1

Follow-up

target_duration Study_Count
12 Months 1
3 Months 1
3 Years 1
40 Years 1
5 Years 1

Overview of Studies

Interventional Trials

#If less then 500 trials

nct_id brief_title link overall_status source primary_completion_date
NCT02376816 Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02376816 Completed Nationwide Children’s Hospital 2017-09-30
NCT03406780 A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03406780 Completed Capricor Inc. 2020-03-10
NCT03375255 A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 in Patients With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03375255 Completed Sarepta Therapeutics, Inc. 2019-08-19
NCT03375164 Systemic Gene Delivery Clinical Trial for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03375164 Active, not recruiting Sarepta Therapeutics, Inc. 2021-04-30
NCT03373968 Givinostat in Duchenne’s Muscular Dystrophy Long-term Safety and Tolerability Study https://ClinicalTrials.gov/show/NCT03373968 Recruiting Italfarmaco 2023-12-31
NCT03362502 A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03362502 Recruiting Pfizer 2021-08-26
NCT03340675 Oral Ifetroban in Subjects With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03340675 Recruiting Cumberland Pharmaceuticals 2023-07-31
NCT03333590 Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03333590 Active, not recruiting Nationwide Children’s Hospital 2020-11-30
NCT03238235 Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03238235 Recruiting Italfarmaco 2020-05-31
NCT03236662 (-)- Epicatechin Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03236662 Completed University of California, Davis 2017-11-30
NCT03218995 Study of Eteplirsen in Young Patients With DMD Amenable to Exon 51 Skipping https://ClinicalTrials.gov/show/NCT03218995 Active, not recruiting Sarepta Therapeutics, Inc. 2021-03-15
NCT03179631 Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03179631 Recruiting PTC Therapeutics 2023-09-05
NCT03167255 Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03167255 Active, not recruiting NS Pharma, Inc. 2021-05-31
NCT03127241 User-centred Assistive System for Arm Functions in Neuromuscular Subjects https://ClinicalTrials.gov/show/NCT03127241 Completed Politecnico di Milano 2019-11-30
NCT03067831 Bone Marrow-Derived Autologous Stem Cells for the Treatment of Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03067831 Recruiting Stem Cells Arabia 2021-11-30
NCT03038399 Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03038399 Active, not recruiting ReveraGen BioPharma, Inc. 2020-04-30
NCT03002298 Virtual Reality in Individuals With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03002298 Completed University of Sao Paulo 2016-08-31
NCT02964377 Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory Adolescents https://ClinicalTrials.gov/show/NCT02964377 Completed University of California, Davis 2018-07-31
NCT02891434 Analysis of a Virtual Reality Task in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02891434 Completed University of Sao Paulo 2016-10-31
NCT02851797 Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02851797 Recruiting Italfarmaco 2022-03-31
NCT02847975 Sodium Nitrate to Improve Blood Flow https://ClinicalTrials.gov/show/NCT02847975 Completed Cedars-Sinai Medical Center 2014-12-31
NCT02835079 Treatment Effect of Tamoxifen on Patients With DMD https://ClinicalTrials.gov/show/NCT02835079 Active, not recruiting Hadassah Medical Organization 2020-11-30
NCT02834650 Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMD https://ClinicalTrials.gov/show/NCT02834650 Recruiting University of California, Los Angeles 2021-01-31
NCT02819557 Study of Ataluren in ≥2 to <5 Year-Old Males With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02819557 Completed PTC Therapeutics 2018-02-09
NCT02760264 A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02760264 Completed ReveraGen BioPharma, Inc. 2018-05-01
NCT02752048 A Phase IIa Study of TAS-205 for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02752048 Completed Taiho Pharmaceutical Co., Ltd. 2017-05-15
NCT02740972 Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02740972 Completed NS Pharma, Inc. 2018-03-31
NCT02710591 Rimeporide in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02710591 Completed EspeRare Foundation 2017-12-31
NCT02667483 Study of DS-5141b in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02667483 Active, not recruiting Daiichi Sankyo, Inc. 2020-12-31
NCT02606136 Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Subjects With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02606136 Active, not recruiting FibroGen 2020-04-30
NCT02500381 Study of SRP-4045 and SRP-4053 in DMD Patients https://ClinicalTrials.gov/show/NCT02500381 Recruiting Sarepta Therapeutics, Inc. 2022-05-31
NCT02530905 Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patients https://ClinicalTrials.gov/show/NCT02530905 Completed Sarepta Therapeutics, Inc. 2018-10-03
NCT02516085 Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformin https://ClinicalTrials.gov/show/NCT02516085 Completed University Hospital, Basel, Switzerland 2012-10-31
NCT02485938 HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne) https://ClinicalTrials.gov/show/NCT02485938 Completed Capricor Inc. 2017-09-30
NCT02439216 Phase 1/2 Study in Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02439216 Completed Catabasis Pharmaceuticals 2017-01-12
NCT02434627 Sodium Nitrate for Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02434627 Completed Cedars-Sinai Medical Center 2018-04-30
NCT02432885 Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy Trial https://ClinicalTrials.gov/show/NCT02432885 Completed InCor Heart Institute 2012-06-30
NCT02421523 Strength Training in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02421523 Completed University of Florida 2018-02-15
NCT02420379 Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02420379 Completed Sarepta Therapeutics, Inc. 2018-12-17
NCT02418338 2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy Children https://ClinicalTrials.gov/show/NCT02418338 Completed University Hospital, Montpellier 2017-06-30
NCT02383511 Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diet https://ClinicalTrials.gov/show/NCT02383511 Completed Summit Therapeutics 2015-08-31
NCT02354781 Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02354781 Completed Nationwide Children’s Hospital 2017-11-30
NCT02354352 Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02354352 Completed Ohio State University 2018-05-31
NCT02310906 Phase I/II Study of SRP-4053 in DMD Patients https://ClinicalTrials.gov/show/NCT02310906 Completed Sarepta Therapeutics, Inc. 2019-03-25
NCT02286947 Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02286947 Completed Sarepta Therapeutics, Inc. 2017-04-21
NCT02251600 A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02251600 Completed PTC Therapeutics 2015-10-31
NCT02235844 Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02235844 Completed Allergy and Asthma Consultants, Wichita, Kansas 2017-09-30
NCT02196467 Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) Patients https://ClinicalTrials.gov/show/NCT02196467 Recruiting CHU de Quebec-Universite Laval 2022-01-31
NCT02168114 Magnetic Resonance and Optical Imaging of Dystrophic and Damaged Muscle https://ClinicalTrials.gov/show/NCT02168114 Completed University of Florida 2018-01-08
NCT02167217 Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02167217 Completed Washington University School of Medicine 2017-02-22
NCT02147639 Effects of Sodium Nitrate on Blood Flow in Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02147639 Completed Cedars-Sinai Medical Center 2014-05-31
NCT02090959 An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy https://ClinicalTrials.gov/show/NCT02090959 Completed PTC Therapeutics 2018-06-21
NCT02081625 Exploratory Study of NS-065/NCNP-01 in DMD https://ClinicalTrials.gov/show/NCT02081625 Completed National Center of Neurology and Psychiatry, Japan 2014-11-30
NCT02056808 A Phase 1b Study of SMT C1100 in Subjects With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02056808 Completed Summit Therapeutics 2014-05-31
NCT02255552 Study of Eteplirsen in DMD Patients https://ClinicalTrials.gov/show/NCT02255552 Completed Sarepta Therapeutics, Inc. 2019-06-14
NCT02018731 L-citrulline and Metformin in Becker’s Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02018731 Completed University Hospital, Basel, Switzerland 2014-09-30
NCT03354039 Tamoxifen in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03354039 Recruiting University Hospital, Basel, Switzerland 2020-06-30
NCT01999075 Stacking Exercises Aid the Decline in FVC and Sick Time https://ClinicalTrials.gov/show/NCT01999075 Completed Children’s Hospital of Eastern Ontario 2018-11-22
NCT01995032 L-citrulline and Metformin in Duchenne’s Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01995032 Completed University Hospital, Basel, Switzerland 2015-10-31
NCT01982695 Cardiomyopathy in DMD: Lisinopril vs. Losartan https://ClinicalTrials.gov/show/NCT01982695 Completed Nationwide Children’s Hospital 2012-08-31
NCT01981915 Optimum Insufflation Capacity in NMD https://ClinicalTrials.gov/show/NCT01981915 Completed Universität Duisburg-Essen 2013-02-28
NCT01954940 Whole Body Vibration Therapy in Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01954940 Completed Children’s Hospital of Eastern Ontario 2017-03-31
NCT01921374 Mother-caregivers of Children With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01921374 Completed Federal University of São Paulo 2013-08-31
NCT01874275 Duchenne Muscular Dystrophy Clinical Trial https://ClinicalTrials.gov/show/NCT01874275 Completed Alan Neuromedical Technologies, LLC 2014-09-30
NCT01856868 Use of (-)-Epicatechin in the Treatment of Becker Muscular Dystrophy (Pilot Study) https://ClinicalTrials.gov/show/NCT01856868 Completed University of California, Davis 2018-09-30
NCT01826487 Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01826487 Completed PTC Therapeutics 2015-08-31
NCT01826422 Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients https://ClinicalTrials.gov/show/NCT01826422 Completed Coordinación de Investigación en Salud, Mexico 2017-01-31
NCT01823783 Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01823783 Recruiting University Hospital, Montpellier 2021-01-31
NCT01761292 A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMD https://ClinicalTrials.gov/show/NCT01761292 Completed Italfarmaco 2014-12-31
NCT01648634 Nebivolol for the Prevention of Left Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01648634 Active, not recruiting Assistance Publique - Hôpitaux de Paris 2021-06-30
NCT01645098 Sedation During Muscle Biopsy in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01645098 Completed Nationwide Children’s Hospital 2013-04-30
NCT01603407 Finding the Optimum Regimen for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01603407 Completed University of Rochester 2019-11-30
NCT01580501 PDE Inhibitors in DMD Study (Acute Dosing Study) https://ClinicalTrials.gov/show/NCT01580501 Completed Cedars-Sinai Medical Center 2013-03-31
NCT01557400 Study of Ataluren for Previously Treated Patients With nmDBMD in Europe, Israel, Australia, and Canada https://ClinicalTrials.gov/show/NCT01557400 Completed PTC Therapeutics 2018-01-31
NCT01540604 CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers https://ClinicalTrials.gov/show/NCT01540604 Completed RSPR Pharma AB NA
NCT01540409 Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01540409 Completed Sarepta Therapeutics, Inc. 2016-04-15
NCT01523964 DART Electrical Impedance Myography (EIM) Trial in Duchenne Muscular Dystrophy (DMD) and Healthy Controls https://ClinicalTrials.gov/show/NCT01523964 Completed Dart Therapeutics. LLC 2012-08-31
NCT01521546 Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01521546 Completed Ohio State University 2016-06-30
NCT01519349 Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body Myositis https://ClinicalTrials.gov/show/NCT01519349 Completed Nationwide Children’s Hospital 2017-10-31
NCT01478022 To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20 https://ClinicalTrials.gov/show/NCT01478022 Completed Parent Project, Italy 2016-03-31
NCT01462292 A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT01462292 Completed GlaxoSmithKline 2013-05-21
NCT01396239 Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients https://ClinicalTrials.gov/show/NCT01396239 Completed Sarepta Therapeutics, Inc. 2012-02-29
NCT01388764 Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on Corticosteroids https://ClinicalTrials.gov/show/NCT01388764 Completed Massachusetts General Hospital 2012-05-31
NCT01359670 Tadalafil and Sildenafil for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01359670 Completed Cedars-Sinai Medical Center 2013-05-31
NCT01350154 Effect of Modulating the nNOS System on Cardiac, Muscular and Cognitive Function in Becker Muscular Dystrophy Patients https://ClinicalTrials.gov/show/NCT01350154 Completed Rigshospitalet, Denmark 2013-04-30
NCT01335295 Safety Study of Flavocoxid in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01335295 Completed University of Messina 2013-12-31
NCT04240314 AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications. https://ClinicalTrials.gov/show/NCT04240314 Enrolling by invitation Nationwide Children’s Hospital 2023-01-15
NCT04179409 A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of Casimersen, Eteplirsen and Golodirsen in Subjects With Duchenne Muscular Dystrophy Carrying Eligible DMD Duplications https://ClinicalTrials.gov/show/NCT04179409 Enrolling by invitation Nationwide Children’s Hospital 2021-09-15
NCT04173234 Aerobic Exercise in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT04173234 Recruiting Hacettepe University 2020-01-15
NCT04129294 Exploratory Study of NS-089/NCNP-02 in DMD https://ClinicalTrials.gov/show/NCT04129294 Enrolling by invitation National Center of Neurology and Psychiatry, Japan 2021-03-31
NCT04060199 Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53) https://ClinicalTrials.gov/show/NCT04060199 Recruiting NS Pharma, Inc. 2024-11-30
NCT04054375 Weekly Steroids in Muscular Dystrophy https://ClinicalTrials.gov/show/NCT04054375 Active, not recruiting Northwestern University 2020-06-01
NCT04004065 Study for Dose Determination of SRP-5051, Then Dose Expansion in Patients With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment https://ClinicalTrials.gov/show/NCT04004065 Recruiting Sarepta Therapeutics, Inc. 2021-08-31
NCT03992430 A Study to Compare Safety and Efficacy of a High Dose of Eteplirsen in Duchenne Muscular Dystrophy (DMD) Patients (MIS51ON) https://ClinicalTrials.gov/show/NCT03992430 Recruiting Sarepta Therapeutics, Inc. 2024-10-31
NCT03985878 A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03985878 Enrolling by invitation Sarepta Therapeutics, Inc. 2026-11-30
NCT03936894 Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03936894 Recruiting Children’s National Research Institute 2020-04-30
NCT03917719 An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03917719 Enrolling by invitation Catabasis Pharmaceuticals 2022-06-30
NCT03879304 Effectiveness of a Multimodal Physiotherapy Program With Virtual Reality Glasses in Duchenne and Becker. https://ClinicalTrials.gov/show/NCT03879304 Enrolling by invitation University of Malaga 2020-12-31
NCT03796637 A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren https://ClinicalTrials.gov/show/NCT03796637 Completed PTC Therapeutics 2019-05-24
NCT03789734 Safety Study of BLS-M22 in Healthy Volunteers https://ClinicalTrials.gov/show/NCT03789734 Recruiting BioLeaders Corporation 2020-06-30
NCT03779646 Bisoprolol in DMD Early Cardiomyopathy https://ClinicalTrials.gov/show/NCT03779646 Recruiting Peking Union Medical College Hospital 2020-07-01
NCT03777319 Spironolactone Versus Prednisolone in DMD https://ClinicalTrials.gov/show/NCT03777319 Recruiting Nationwide Children’s Hospital 2021-12-31
NCT03769116 A Randomized, Double-blind, Placebo-controlled Study of SRP-9001 for Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03769116 Active, not recruiting Sarepta Therapeutics, Inc. 2022-10-10
NCT03760029 A Natural History Study In Chinese Male Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03760029 Recruiting Pfizer 2022-09-24
NCT03703882 Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03703882 Active, not recruiting Catabasis Pharmaceuticals 2020-06-30
NCT03675126 An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 https://ClinicalTrials.gov/show/NCT03675126 Recruiting Sarepta Therapeutics, Inc. 2024-07-31
NCT03648827 A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) https://ClinicalTrials.gov/show/NCT03648827 Active, not recruiting PTC Therapeutics 2020-06-30
NCT03611244 Prevention of Scoliosis in Patients With Duchenne Muscular Dystrophy Using Portable Seat Device https://ClinicalTrials.gov/show/NCT03611244 Recruiting Seoul National University Hospital 2024-12-31
NCT03541070 The Effect of Kinesiology Taping on Balance in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03541070 Completed Hacettepe University 2017-09-15
NCT03531788 Use of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMD https://ClinicalTrials.gov/show/NCT03531788 Active, not recruiting University of Pittsburgh 2020-12-31
NCT03529240 Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy Consumption https://ClinicalTrials.gov/show/NCT03529240 Completed Hacettepe University 2017-08-05
NCT03508947 Safety and Tolerability of WVE-210201 in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03508947 Completed Wave Life Sciences Ltd. 2019-03-06
NCT03490214 Non-invasive Imaging of Muscle Structure in Duchenne Muscular Dystrophy Using Multispectral Optoacoustic Tomography https://ClinicalTrials.gov/show/NCT03490214 Completed University of Erlangen-Nürnberg Medical School 2018-08-01
NCT01247207 Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD) https://ClinicalTrials.gov/show/NCT01247207 Enrolling by invitation PTC Therapeutics 2020-12-31
NCT01183767 Sunphenon Epigallocatechin-Gallate (EGCg) in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01183767 Completed Charite University, Berlin, Germany 2018-09-06
NCT01153932 Phase II Doubleblind Exploratory Study of GSK2402968 in Ambulant Subjects With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01153932 Completed GlaxoSmithKline 2012-03-31
NCT01126697 Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies https://ClinicalTrials.gov/show/NCT01126697 Completed Cooperative International Neuromuscular Research Group 2017-12-31
NCT01070511 Tadalafil in Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01070511 Completed Cedars-Sinai Medical Center 2012-12-31
NCT01037309 Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT01037309 Completed BioMarin Pharmaceutical 2013-05-31
NCT01027884 Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT01027884 Completed Santhera Pharmaceuticals 2014-01-31
NCT00873782 Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00873782 Completed University of North Carolina, Chapel Hill 2014-02-28
NCT01254019 A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01254019 Completed GlaxoSmithKline 2013-06-28
NCT00844597 Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients https://ClinicalTrials.gov/show/NCT00844597 Completed Sarepta Therapeutics, Inc. 2010-06-30
NCT03603288 Phase III Study With Idebenone in Patients With Duchenne Muscular Dystrophy (SIDEROS-E) https://ClinicalTrials.gov/show/NCT03603288 Recruiting Santhera Pharmaceuticals 2023-12-31
NCT02814019 A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroids https://ClinicalTrials.gov/show/NCT02814019 Active, not recruiting Santhera Pharmaceuticals 2021-08-31
NCT02760277 An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT02760277 Completed ReveraGen BioPharma, Inc. 2018-04-26
NCT03532542 An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03532542 Enrolling by invitation Sarepta Therapeutics, Inc. 2026-08-10
NCT02295748 An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort https://ClinicalTrials.gov/show/NCT02295748 Completed PTC Therapeutics 2017-08-24
NCT02246478 A Study of TAS-205 for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02246478 Completed Taiho Pharmaceutical Co., Ltd. 2015-06-30
NCT03439670 A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03439670 Recruiting ReveraGen BioPharma, Inc. 2020-05-01
NCT00758225 Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension) https://ClinicalTrials.gov/show/NCT00758225 Completed Santhera Pharmaceuticals 2011-01-31
NCT00654784 Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00654784 Completed Santhera Pharmaceuticals 2007-08-31
NCT00592553 Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) https://ClinicalTrials.gov/show/NCT00592553 Completed PTC Therapeutics 2009-12-31
NCT00451074 Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons https://ClinicalTrials.gov/show/NCT00451074 Completed Nationwide Children’s Hospital 2009-07-31
NCT00428935 Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00428935 Completed Nationwide Children’s Hospital 2009-03-31
NCT00296621 Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00296621 Completed Assistance Publique - Hôpitaux de Paris 2008-02-29
NCT00264888 Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00264888 Completed PTC Therapeutics 2007-05-31
NCT00243789 Study of Daily Pentoxifylline as a Rescue Treatment in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00243789 Completed Cooperative International Neuromuscular Research Group 2007-12-31
NCT00159250 Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00159250 Completed Imperial College London 2008-12-31
NCT00110669 High-dose Prednisone in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00110669 Completed Cooperative International Neuromuscular Research Group 2007-12-31
NCT00104078 Study Evaluating MYO-029 in Adult Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00104078 Completed Wyeth is now a wholly owned subsidiary of Pfizer NA
NCT00102453 Pentoxifylline in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00102453 Completed Cooperative International Neuromuscular Research Group 2006-07-31
NCT00005574 Gentamicin Treatment of Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00005574 Completed National Institutes of Health Clinical Center (CC) NA
NCT00033813 KUL0401: An Open-label Pilot Study of Oxatomide in Steroid-Naive Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00033813 Completed Cooperative International Neuromuscular Research Group 2006-12-31
NCT00033189 An Open-label Pilot Study of Coenzyme Q10 in Steroid-Treated Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00033189 Completed Cooperative International Neuromuscular Research Group NA
NCT00018109 A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT00018109 Completed National Center for Research Resources (NCRR) NA
NCT00004646 Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00004646 Completed Office of Rare Diseases (ORD) NA
NCT00016653 Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00016653 Completed Cooperative International Neuromuscular Research Group NA

Observational Studiess

#If less then 500 studies

nct_id brief_title link overall_status source primary_completion_date
NCT03319030 Aerobic Exercise in Boys With Duchenne Muscular Dystrophy (DMD) https://ClinicalTrials.gov/show/NCT03319030 Completed Ann & Robert H Lurie Children’s Hospital of Chicago 2018-04-30
NCT02994030 Biomarker for Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02994030 Recruiting Centogene AG Rostock 2023-12-31
NCT02972580 Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD https://ClinicalTrials.gov/show/NCT02972580 Active, not recruiting Nationwide Children’s Hospital 2020-12-31
NCT02571205 Testosterone Therapy for Pubertal Delay in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02571205 Active, not recruiting Newcastle-upon-Tyne Hospitals NHS Trust 2019-02-28
NCT02195999 Assessment of Cardiopulmonary Function in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02195999 Completed University of Florida 2019-03-06
NCT02194725 Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02194725 Completed National Institutes of Health Clinical Center (CC) 2015-04-20
NCT02165358 Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I https://ClinicalTrials.gov/show/NCT02165358 Completed Rigshospitalet, Denmark 2015-01-31
NCT02034305 Peak Cough Flow and Cough Clearance in Patients With Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02034305 Recruiting University of Pittsburgh 2021-01-31
NCT01931644 At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions https://ClinicalTrials.gov/show/NCT01931644 Recruiting Sanguine Biosciences 2025-08-31
NCT01633866 Pediatric Radio Frequency Coils Generic https://ClinicalTrials.gov/show/NCT01633866 Active, not recruiting Children’s Hospital Medical Center, Cincinnati 2022-06-30
NCT01506518 Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01506518 Active, not recruiting University of North Carolina, Chapel Hill 2020-09-30
NCT01491555 Electrical Impedance Myography and Ultrasound as Biomarkers of Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01491555 Completed Boston Children’s Hospital 2015-09-30
NCT01484678 Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01484678 Active, not recruiting University of Florida 2021-08-31
NCT01451281 Studying Skeletal Muscle, Heart, and Diaphragm Imaging in Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01451281 Completed National Institutes of Health Clinical Center (CC) NA
NCT01380964 Research of Biomarkers in Duchenne Muscular Dystrophy Patients https://ClinicalTrials.gov/show/NCT01380964 Completed Genethon 2015-12-31
NCT04384354 Digestive Events in Duchenne Muscular Dystrophy Patients https://ClinicalTrials.gov/show/NCT04384354 Completed Centre d’Investigation Clinique et Technologique 805 2018-12-31
NCT04349566 Fast Troponin as a Biomarker to Assess Exercise-induced Muscle Damage in Muscle Diseases https://ClinicalTrials.gov/show/NCT04349566 Enrolling by invitation Rigshospitalet, Denmark 2020-12-31
NCT04287582 The Evaluation of Muscle Activation in Climbing up Stairs Activity in Children With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT04287582 Recruiting Hacettepe University 2020-03-07
NCT04254172 A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT04254172 Recruiting Pfizer 2021-08-12
NCT04193085 Wearable Technology to Assess Gait Function in SMA and DMD https://ClinicalTrials.gov/show/NCT04193085 Recruiting Columbia University 2020-12-31
NCT04012671 A Registered Cohort Study on Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT04012671 Recruiting First Affiliated Hospital of Fujian Medical University 2039-12-31
NCT03882827 Natural History of Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03882827 Recruiting Genethon 2022-06-30
NCT03786913 Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular Diseases https://ClinicalTrials.gov/show/NCT03786913 Completed Benha University 2019-02-02
NCT03680365 Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of Families https://ClinicalTrials.gov/show/NCT03680365 Completed Jett Foundation, Inc. 2019-03-15
NCT03589612 Regression of Hamstring Flexibility and Performance in Children With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03589612 Completed Hacettepe University 2019-01-24
NCT03589573 Effect of Muscle Strength on Hamstring Flexibility in Children With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03589573 Completed Hacettepe University 2017-09-25
NCT03552874 Pulmonary and Upper Limb Functions in Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03552874 Completed Hacettepe University 2017-07-31
NCT03534349 Lower Limb Flexibility in Duchenne Muscular Dystrophy: Effects on Functional Performance https://ClinicalTrials.gov/show/NCT03534349 Completed Hacettepe University 2017-06-30
NCT03521271 Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03521271 Completed Hacettepe University 2018-01-26
NCT03513367 The Validation Process for Confirmation of the French Version of the Pediatric Quality of Life Inventory :PedsQLTM. https://ClinicalTrials.gov/show/NCT03513367 Recruiting University Hospital, Toulouse 2019-09-19
NCT01182324 The PTC124 (Ataluren) Clinical Trial for Duchenne Muscular Dystrophy: Exploration of the Experiences of Parents, Clinician Researchers, and the Industry Sponsor https://ClinicalTrials.gov/show/NCT01182324 Completed National Institutes of Health Clinical Center (CC) NA
NCT01125709 Comparative Study of Clinical Endpoint in DMD: Handheld Myometry (HHM) Versus CINRG Quantitative Measurement System (CQMS) https://ClinicalTrials.gov/show/NCT01125709 Completed Cooperative International Neuromuscular Research Group 2010-06-30
NCT01098708 This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01098708 Completed Washington University School of Medicine 2013-11-30
NCT01081080 Cardiac Magnetic Resonance in Children With Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01081080 Completed Cooperative International Neuromuscular Research Group 2011-10-31
NCT01066455 Cardiac Outcome Measures in Children With Muscular Dystrophy https://ClinicalTrials.gov/show/NCT01066455 Completed Cooperative International Neuromuscular Research Group 2012-05-31
NCT00893334 Evaluation of Limb-Girdle Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00893334 Completed Cooperative International Neuromuscular Research Group 2013-12-31
NCT03951675 The Burden of Access in Duchenne Muscular Dystrophy in the US https://ClinicalTrials.gov/show/NCT03951675 Recruiting University of Florida 2020-06-30
NCT02470962 Cardiac Involvement in Patients With Duchenne/Becker Muscular Dystrophy https://ClinicalTrials.gov/show/NCT02470962 Active, not recruiting University Children’s Hospital, Zurich 2020-04-30
NCT01712152 Myocardial Involvement in Carriers of Duchenne Muscular Dystrophy: An MRI-study https://ClinicalTrials.gov/show/NCT01712152 Completed Hospital Rudolfstiftung 2014-04-30
NCT03947112 Physical Activity Level of Norwegian Boys With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT03947112 Recruiting Haukeland University Hospital 2021-03-30
NCT00390104 Molecular Analysis of Patients With Neuromuscular Disease https://ClinicalTrials.gov/show/NCT00390104 Recruiting Boston Children’s Hospital 2025-12-31
NCT00312247 Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy https://ClinicalTrials.gov/show/NCT00312247 Completed Shriners Hospitals for Children 2014-12-31

Registries

#If less then 500 registries

nct_id brief_title link overall_status source primary_completion_date
NCT02369731 Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) https://ClinicalTrials.gov/show/NCT02369731 Recruiting PTC Therapeutics 2025-05-30
NCT02340923 A Device for Rapid, Painless, Bedside Muscle Evaluation of Children https://ClinicalTrials.gov/show/NCT02340923 Completed Skulpt, Inc. 2016-06-30
NCT02069756 The Duchenne Registry https://ClinicalTrials.gov/show/NCT02069756 Recruiting The Duchenne Registry 2027-10-31
NCT01963897 Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life. https://ClinicalTrials.gov/show/NCT01963897 Completed Oslo University Hospital 2017-06-30
NCT04120168 Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease https://ClinicalTrials.gov/show/NCT04120168 Recruiting Turkish Society of Pediatric Gastroenterology, Hepatology and Nutrition 2020-03-31